Identification of pharmacological chaperones as new therapeutic agents to treat phenylketonuria.

A.L. Pey, M. Ying, N. Cremades, A. Velazquez-Campoy, T. Scherer, B. Thöny, J. Sancho, A. Martinez. Identification of pharmacological chaperones as new therapeutic agents to treat phenylketonuria.. Journal of Clinical Investigation. 2008 118:2858-2867