Therapeutic strategies for Gaucher disease: Miglustat (NB-DNJ) as a pharmacological chaperone for glucocerebrosidase and the different thermostability of Velaglucerase alfa and Imiglucerase

O. Abián, P. Alfonso, A. Velazquez-Campoy, P. Giraldo, M. Pocovi, J. Sancho. Therapeutic strategies for Gaucher disease: Miglustat (NB-DNJ) as a pharmacological chaperone for glucocerebrosidase and the different thermostability of Velaglucerase alfa and Imiglucerase. Molecular Pharmaceutics. 2011 8:2390-2397